Efficacy and safety of risdiplam in patients with type 1 spinal muscular atrophy: a 3-year open-label extension of the two-part, phase 2 FIREFISH trial.

Orphanhood and caregiver loss after Venezuela's earthquake doublet: an overlooked child health crisis.

A national programme of bivalent prefusion F vaccination in pregnancy and protection against respiratory syncytial virus hospitalisation in infants until age 6 months in the UK: a multicentre, prospective, test-negative, case-control study.

Associations between childhood somatic conditions and psychiatric diagnoses in autistic young adults: a retrospective, population-based cohort study in Sweden.

A decade of disease-modifying therapies for spinal muscular atrophy.

From PCOS to PMOS: inclusion of the adolescent voice in setting clinical and research priorities.

Efficacy and safety of risdiplam in patients with type 1 spinal muscular atrophy: a 3-year open-label extension of the two-part, phase 2 FIREFISH trial.

Orphanhood and caregiver loss after Venezuela's earthquake doublet: an overlooked child health crisis.

A national programme of bivalent prefusion F vaccination in pregnancy and protection against respiratory syncytial virus hospitalisation in infants until age 6 months in the UK: a multicentre, prospective, test-negative, case-control study.

Associations between childhood somatic conditions and psychiatric diagnoses in autistic young adults: a retrospective, population-based cohort study in Sweden.

A decade of disease-modifying therapies for spinal muscular atrophy.

From PCOS to PMOS: inclusion of the adolescent voice in setting clinical and research priorities.